Donate to HNRNPH2 Research
Funds raised by YBRP will be used to further the three main goals which comprise our mission:
- to fund research to identify, understand, treat, and ultimately cure those impacted by HNRNPH2 mutations;
- to fund initiatives to raise awareness and identify more individuals with HNRNPH2 mutations; and
- to connect families impacted by HNRNPH2 in order to contribute to the understanding of the disorder.
Our Research and Fundraising Goals
In 2020, YBRP awarded our research grant to Andlit Therapeutics and completed the funding of year two of this project in July 2021. But that is not the end of our journey! Completion of this initial project places us at the "Disease Concept/Disease Burden" phase of the overall process to reach clinical trials, as illustrated below. The next steps are to fund a series of research projects to identify outcome measures and conduct efficacy & toxicity tests, with a total estimated cost of $1.4M - $1.8M. This research once completed would place us in the "Mechanisms ID'd" phase of the clinical trial process. Our goal now is to raise $300,000-$500,000 to fund research projects to identify outcome measures and the development of a drug for rodent and cell line testing, the next phases toward reaching clinical trials.
YBRP maintains minimal overhead and operating expenses and all board members and officers are volunteers, no board member or officer receives any compensation for their services. Approximately 70% of funds raised are dedicated to funding research, 20% to patient engagement/outreach & raising awareness, and 5% to operating expenses.
YBRP is an approved 501(c)(3) non-profit organization. EIN 83-4191901